BSGCT Public & Patient Series: Gene Therapy
The BSGCT Public and Patient Engagement Subcommittee are organising a series of talks designed to provide a lay introduction and background to the rapidly developing world of gene and cell therapy.
NEXT EVENT
Gene Therapy
19:30 CET, Wednesday 19th January 2022.
Dr Simon N Waddington, University College London
The past two years have witnessed such upheaval that the word “unprecedented” seems inadequate. Hitherto unimaginable occurrences are now accepted with little discussion. One of these events was the successful treatment of more than one tenth of the population of the world with genetic therapy. This was, of course, the use of vaccination, using mRNA or adenovirus, to raise immunity to SARS-CoV2. Aside from this stupendous achievement, we now live in a world where previously untreatable diseases such as Spinal Muscular Atrophy Type I are being cured with single intravenous injections of gene therapy vectors. In this talk, I will discuss some of the technologies underpinning this revolution, I will discuss some of the success stories, and where challenges still lie and where we might see advances being made.